Nationwide Children Symposium on Sickle Cell Disease 2022

Nationwide Children Symposium on Sickle Cell Disease 2022

Include: 5 videos + 5 pdfs, size: 2.12 GB

Friday, November 11, 2022, 8:00 AM – 3:40 PM, Nationwide Children’s Hospital Conference Center, Columbus, OH

This symposium will provide information to our regional colleagues and our patients and families on current clinical trials and advances in the field of Disease Modifying Therapies (DMT), Stem Cell Transplantation (SCT) and Gene Therapy in Sickle Cell Disease (SCD). The aim of this symposium is to critically analyze and review the pros and cons of these newer treatments including curative options.

The Nationwide Children Symposium on Sickle Cell Disease 2022 was designed for a diverse group of healthcare professionals. The target audience included specialists in Blood & Marrow Transplantation (BMT), Hematology, and Hematology/Oncology. The symposium aimed to provide information on current clinical trials and advances in disease-modifying therapies, stem cell transplantation, and gene therapy for sickle cell disease

1. Review current and upcoming disease modifying drugs for SCD such as crizanlizumab, voxelotor, glutamine and others that are in the pipeline.
2. Compare the different alternative donor (non-sibling) choices for HCT in SCD and recent developments in matched sibling donor transplant for SCD
3. Discuss the advances in gene therapy for SCD
4. Analyze the long-term effects of all available therapies including curative options; review current data on risk for malignancies and infertility in patient with SCD